AN UNBIASED VIEW OF MUSCULAR DYSTROPHY THERAPIES VASANT KUNJ

Limb-girdle muscular dystrophies can either be autosomal dominant (single gene defect on a chromosome from both mother or father or a single duplicate of the mutant gene and one particular normal gene, often known as kind 1 LGMD) or autosomal recessive (a defect or mutation to the gene within the chromosome of each and every mother or father is nee